Biogen’s salanersen is now heading into three Phase III trials in SMA.

Globally, Spinal Muscular Atrophy (SMA), a rare genetic neuromuscular disorder, affects approximately 1 in 10,000 live births ...

Early diagnosis and treatment of SMA can limit disease progression in children and adults, extending life expectancy and improving QOL. Spinal muscular atrophy (SMA) is a severe genetic condition that ...

University of Pittsburgh School of Medicine researchers carrying out a small pilot clinical trial demonstrating that a drug-free, minimally invasive intervention targets the root cause of progressive ...

HONOLULU (KITV4) -- Oahu student and artist Janelle Fiesta, 26, has been living with spinal muscular atrophy (SMA), a rare, progressive neuromuscular disease, her entire life. She is the first person ...

- Taldefgrobep alfa, a myostatin-targeting biologic investigational agent, in Phase 3 development to increase muscle mass for Spinal Muscular Atrophy patients now granted Fast Track in addition to ...

Children with spinal muscular atrophy (SMA), a rare autosomal recessive disease that results in progressive muscle weakness and atrophy, can suffer the concerning consequences of dysphagia, which ...

PITTSBURGH (KDKA) -- August is SMA Awareness Month. SMA stands for Spinal Muscular Atrophy. It is a rare neuromuscular disorder that starts in the central nervous system and affects all of the muscles ...

Footballer Ezekiel Otuoma and his wife Rachael Otuoma. Otuoma died after a long battle with Motor Neurone Disease (MND). [File, Standard] Former AFC Leopards winger Ezekiel Otuoma passed away at the ...